Mixed-Phenotype Acute Leukemia Transforming Into Acute Myelomonocytic Leukemia (AML M4): A Case Report and Therapeutic Challenges.

Mixed-Phenotype Acute Leukemia Transforming Into Acute Myelomonocytic Leukemia (AML M4): A Case Report and Therapeutic Challenges.

Publication date: Nov 01, 2025

Mixed-phenotype acute leukemia (MPAL) accounts for a fraction of de novo acute leukemias and carries a dismal prognosis, especially when adverse lesions such as monosomy 7 are present. Consensus on optimal frontline therapy remains lacking. Herein, we present a 69-year-old woman who presented with pancytopenia and 79% circulating blasts. Immunophenotyping and cytogenetics established T/myeloid MPAL with a hypodiploid clone 45, XX, dic(7;12)(p11. 2;p13)(19)/46,XX and an IDH2 R140Q mutation. Hyperfractionated cyclophosphamide, vincristine, doxorubicin, and dexamethasone (Hyper-CVAD) induction achieved morphological complete remission, but measurable residual disease (MRD) persisted. Consolidation with mini-cyclophosphamide, vincristine, and dexamethasone (mini-CVD) and prednisone, vincristine, methotrexate, and 6-mercaptopurine (POMP) maintenance failed to eradicate MRD, and overt relapse occurred at month 7. Nelarabine salvage was initiated. After two nelarabine cycles (month 8. 5), bone marrow contained 85% myelomonocytic blasts. Cytogenetic evolution to 45,XX,psu dic(7;12)(p11. 2;p11. 2)/45,idem,del(16)(q12) marked transformation to acute myelomonocytic leukemia (AML-M4). Profound pancytopenia led to invasive pulmonary aspergillosis and symptomatic severe acute respiratory syndrome coronavirus 2 (SARS-CoV-2) infection. With refractory disease and escalating infectious morbidity, active therapy was discontinued; the patient died 11 months after diagnosis. This case illustrates rapid clonal evolution of T/myeloid MPAL into chemoresistant AML-M4 driven by persistent chromosome-7 loss and acquisition of del(16q). Early molecular risk stratification and deployment of targeted agents, venetoclax-based combinations, or timely allogeneic transplantation should be considered before irreversible genomic complexity emerges. Prospective studies tailored to high-risk cytogenetic subsets of MPAL are urgently needed.

Open Access PDF

Concepts Keywords
45idemdel16q12 clonal evolution
Immunophenotyping lineage switch relapse
Leukemia minimal residual disease
M4 mixed-phenotype acute leukemia
Timely myeloid transformation
precision oncology

Semantics

Type Source Name
disease MESH Acute Myelomonocytic Leukemia
disease MESH AML
disease MESH monosomy 7
disease MESH pancytopenia
drug DRUGBANK Dacarbazine
drug DRUGBANK Cyclophosphamide
drug DRUGBANK Vincristine
drug DRUGBANK Doxorubicin
drug DRUGBANK Dexamethasone
drug DRUGBANK Prednisone
drug DRUGBANK Methotrexate
drug DRUGBANK Mercaptopurine
disease MESH relapse
drug DRUGBANK Nelarabine
disease MESH invasive pulmonary aspergillosis
disease MESH severe acute respiratory syndrome
disease MESH infection
drug DRUGBANK Venetoclax
pathway REACTOME Reproduction
drug DRUGBANK Coenzyme M
disease MESH monosomy
disease MESH SARS CoV 2 infection
disease MESH minimal residual disease
disease MESH acute lymphoblastic leukemia
pathway KEGG Acute myeloid leukemia
pathway REACTOME Methylation
disease MESH CKs
disease MESH CAP
disease MESH partial monosomy
disease MESH hypertension
disease MESH subdural hematoma
disease MESH fatigue
disease MESH anemia
disease MESH neutropenia
disease MESH thrombocytopenia
disease MESH Tumor
drug DRUGBANK Uric Acid
drug DRUGBANK Creatinine
disease MESH Inflammation
drug DRUGBANK Iron
drug DRUGBANK Hepatitis B Vaccine (Recombinant)
drug DRUGBANK Prothrombin
disease MESH tumor lysis syndrome
disease MESH tricuspid regurgitation
disease MESH bacteremia
disease MESH cytopenias
disease MESH deep vein thrombosis
disease MESH air crescent sign
disease MESH Pre B ALL
disease MESH Park
disease MESH death
drug DRUGBANK Blinatumomab
disease MESH myeloid sarcoma
disease MESH APL
drug DRUGBANK Cytarabine
disease MESH leukemias
disease MESH eosinophilia
disease MESH syndromes
disease MESH biphenotypic acute leukemia
disease MESH chromosomal abnormalities
disease MESH Dis
drug DRUGBANK Enasidenib
drug DRUGBANK Decitabine
disease MESH CAR
drug DRUGBANK Guanosine
disease MESH hematological malignancies
disease MESH cas
disease MESH acute monocytic leukemia
disease MESH Lymphoma
disease MESH pbc
disease MESH myeloid leukemia

Original Article

(Visited 5 times, 1 visits today)

Leave a Comment

Your email address will not be published. Required fields are marked *